Date of Award

Spring 4-3-2023

Embargo Period

4-3-2025

Document Type

Thesis

Degree Name

Doctor of Philosophy (PhD)

Department

Biochemistry

Additional Department

Pediatrics

College

College of Graduate Studies

Additional College

College of Medicine

First Advisor

Denis C. Guttridge

Abstract

Rhabdomyosarcoma (RMS) is the most common soft tissue cancer among

children, characterized by a skeletal muscle lineage that is impaired from

undergoing terminal differentiation. NF-κB is constitutively active in cancer cells

and plays a critical role in cell survival. Although NF-κB is also activated in RMS,

surprisingly we find that these tumors are less dependent on NF-κB to overcome

stress-induced cell death. Instead, RMS cells survive by being partially

differentiated under the control of the myogenic transcription factor MyoD. Loss of

MyoD or cellular reprogramming dedifferentiates RMS tumor cells and promotes

cell death when exposed to stress. Further, use of a CRISPR screen identified the

tumor suppressor gene, CYLD, controlled by MyoD mediated DNA

methyltransferase activity to regulate RMS survival. Together, results reveal

oncogenic functions of MyoD that enhance RMS survival through pro-differentiation

and anti-cell death activities; findings that challenge the long existing

paradigm of MyoD in RMS pathogenesis.

Rights

Copyright is held by the author. All rights reserved.

Available for download on Thursday, April 03, 2025

Share

COinS